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SPINAL MUSCULAR ATROPHY

Spinal Muscular Atrophy Recruitment

Specialized recruitment for SMA gene therapy and treatment trials with comprehensive neuromuscular expertise.

220+
SMA Patients Successfully Recruited
8+
Completed SMA Studies
69%
Faster Enrollment Than Industry Average
97%
Patient Retention Rate in SMA Trials

Spinal Muscular Atrophy Specializations

Comprehensive recruitment strategies for all types and stages of spinal muscular atrophy.

SMA Type 1 (Severe)

Infantile-onset with most severe motor impairment

  • Gene therapy trials
  • Respiratory support studies
  • Early intervention protocols

SMA Type 2 (Intermediate)

Childhood-onset with moderate motor function

  • Functional improvement studies
  • Mobility preservation
  • Quality of life trials

SMA Type 3 (Mild)

Later-onset with ambulatory function

  • Walking preservation
  • Strength maintenance
  • Long-term outcomes

SMA Type 4 (Adult-Onset)

Adult presentation with mild symptoms

  • Progression monitoring
  • Work capacity studies
  • Family planning research

Pre-Symptomatic SMA

Genetically confirmed but not yet symptomatic

  • Prevention studies
  • Early treatment trials
  • Natural history research

SMA with Respiratory Issues

Patients requiring ventilatory support

  • Respiratory function studies
  • Ventilation optimization
  • Pulmonary care trials

Ready to Accelerate Your SMA Clinical Trial?

Partner with our expert team to access our specialized network of spinal muscular atrophy patients and families.