Pompe Disease Patient Recruitment in Hawaii

TheraNovex connects clinical trial sponsors with pre-screened, eligible Pompe Disease patients across Hawaii, including Honolulu, Pearl City, Hilo, and beyond.

Pompe disease patient recruitment for late-onset and classic infantile ERT and next-generation therapy trials.

Who qualifies: Patients with confirmed Pompe disease (GAA mutation) including late-onset and ERT-experienced patients.

Recruitment challenges: GAA mutation confirmation and acid alpha-glucosidase enzyme activity requirements.

Our approach: Metabolic disease center networks and Pompe patient advocacy partnerships.

Our recruitment network spans all major metropolitan areas in Hawaii, ensuring broad geographic coverage for your Pompe Disease trial.