Duchenne Muscular Dystrophy Patient Recruitment in Pennsylvania
TheraNovex connects clinical trial sponsors with pre-screened, eligible Duchenne Muscular Dystrophy patients across Pennsylvania, including Philadelphia, Pittsburgh, Allentown, and beyond.
DMD patient recruitment for exon-skipping, gene therapy, and corticosteroid clinical trials.
Who qualifies: Males aged 4–18 with confirmed DMD (dystrophin mutation), ambulatory and non-ambulatory.
Recruitment challenges: Dystrophin mutation confirmation and ambulatory status requirements.
Our approach: Neuromuscular disease center networks, Parent Project Muscular Dystrophy partnerships.
Our recruitment network spans all major metropolitan areas in Pennsylvania, ensuring broad geographic coverage for your Duchenne Muscular Dystrophy trial.