Duchenne Muscular Dystrophy Clinical Trial Patient Recruitment

DMD patient recruitment for exon-skipping, gene therapy, and corticosteroid clinical trials.

Who qualifies: Males aged 4–18 with confirmed DMD (dystrophin mutation), ambulatory and non-ambulatory.

Recruitment challenges: Dystrophin mutation confirmation and ambulatory status requirements.

Our approach: Neuromuscular disease center networks, Parent Project Muscular Dystrophy partnerships.