180+
DMD Patients Successfully Recruited
9+
Completed Duchenne Studies
72%
Faster Enrollment Than Industry Average
98%
Patient Retention Rate in DMD Trials
Duchenne MD Recruitment Specializations
Comprehensive recruitment strategies for all stages and manifestations of Duchenne muscular dystrophy.
Ambulatory DMD
Boys with DMD who are still walking independently
- Gene therapy trials
- Exon skipping studies
- Functional preservation
Non-Ambulatory DMD
Wheelchair-dependent patients with advanced disease
- Respiratory support studies
- Cardiac protection
- Quality of life interventions
Early/Presymptomatic DMD
Young boys with confirmed diagnosis but minimal symptoms
- Prevention studies
- Early intervention
- Biomarker research
Steroid-Naive DMD
Patients not yet started on corticosteroid therapy
- Steroid comparison studies
- Alternative anti-inflammatory
- Natural history studies
DMD with Cardiomyopathy
Patients with cardiac involvement requiring specialized care
- Cardiac protection studies
- Heart function monitoring
- Combination therapies
Becker Muscular Dystrophy
Milder form of dystrophin deficiency with later onset
- Progression studies
- Functional assessments
- Long-term outcomes